Major Drugs - Cambridge, MA, US
FoldRx Pharmaceuticals is a development and discovery company focusing on first-in-class, disease-modifying, small molecule therapeutics to treat diseases of protein misfolding. The folding and maintenance of proteins in a correctly folded active form is essential to normal cellular function.Accumulation of misfolded proteins, due to mutations or to defects in cellular quality control mechanisms, can prevent them from performing their normal function or result in toxic intermediates.